• Click on a protocol’s title to view its description in ClinicalTrials.gov.
  • Click on (pdf) to view the protocol (WUSTL key password required).
Atypical HUS
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
Atypical Hemolytic-Uremic Syndrome (aHUS) Registry (Alexion)Open to enrollment
Bleeding and clotting disorders
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Bill Berger
bergerwb@wustl.edu
314-362-9996
CDC Community Counts: Surveillance Project for Patients with Bleeding and Blood Clotting Disorders (CDC Division of Blood Disorders)Open
Blood clots in cancer patients
PI / ContactProtocol (Sponsor)Status
PI: Kristen Sanfilippo
Contact: Kim Kramer
kramerka@wustl.edu
314-273-1790
A multicenter, randomized, open-label, blinded endpoint evaluation, phase 3 study comparing the effects of abelacimab relative to apixaban on venous thromboembolism (VTE) recurrence and bleeding in patients with cancer associated VTE (ANT-007) (Anthos Therapeutics)Open to enrollment
(pdf – password protected)
PI: Kristen Sanfilippo
Contact: Kim Kramer
kramerka@wustl.edu
314-273-1790
A multicenter, randomized, open-label, blinded endpoint evaluation, phase 3 study comparing the effect of abelacimab relative to dalteparin on venous thromboembolism (VTE) recurrence and bleeding in patients with gastrointestinal (GI) / genitourinary (GU) cancer associated VTE (ANT-008) (Anthos Therapeutics)Open to enrollment
(pdf – password protected)
Essential Thrombocythemia
PI / ContactProtocol (Sponsor)Status
PI: Stephen Oh
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 3 Study of P1101 vs Anagrelide in Essential Thrombocythemia Patients who Failed Hydroxyurea (P1101ET) (PharmaEssentia Corp)Open to enrollment
(pdf – password protected)
PI: Stephen Oh
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 2b Open Label Study of Ropeginterferon (P1101) in Essential Thrombocythemia Patients (PharmaEssentia)Pending Open
(pdf – password protected)
Hemophilia A
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Rachel Cody
rcody@wustl.edu
314-362-7306
A Phase 3 Study of Valoctocogene Roxaparvovec in Hemophilia A Patients (BioMarin Pharmaceutical)Open
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
Emicizumab In Patients With Acquired Hemophilia A: Multicenter, Single-Arm, Open-Label Clinical Trial (Genetech)Enrollment pending
(pdf – password protected)
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
Efficacy and Safety of Concizumab prophylaxis in patients with haemophilia A or B with inhibitors (Novo Nordisk Pharmaceuticals, Inc.)Open to enrollment
(pdf – password protected)
Hemophilia/Bleeding
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Bill Berger
bergerwb@wustl.edu
314-362-9996
American Thrombosis and Hemostasis Network Data Collection (CDC Division of Blood Disorders)Open
Myelofibrosis
PI / ContactProtocol (Sponsor)Status
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
Extended Access of Momelotinib in Adults with Myelofibrosis (352-4365) (Gilead)Enrolling by invitation only
(pdf – password protected)
PI: Stephen Oh
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 2 Dose Expansion Study of CPI-0610 with and without Ruxolitinib in Patients with Myelofibrosis (MANIFEST) (Constellation Pharmaceuticals)Ongoing; closed to enrollment
(pdf – password protected)
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
Phase 2 Study of KRT-232 in Myelofibrosis Patients Who Failed Prior JAK Inhibitor (Kartos Therapeutics)Open to enrollment
(pdf – password
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
A Phase 1/2 study of INCB000928 ± Ruxolitinib in Myelofibrosis Patients with Anemia (INCB 00928-104) (Incyte Corp)Open to enrollment
(pdf – password protected)
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
A Phase 3 Study of Pelabresib (CPI-0610) plus Ruxolitinib vs Placebo plus Ruxolitinib in Myelofibrosis Patients (Constellation Pharmaceuticals)Ongoing; closed to enrollment
(pdf – password protected)
PI: Amy Zhou
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 1b/2a Study of DISC-0974 in Myelofibrosis Patients with Anemia (DISC-0974-102) (DISC Medicine)Pending open
(pdf – password protected)
PNH
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry (Alexion)Open to enrollment
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
A multicenter, single arm, open-label trial to evaluate efficacy and safety of oral, twice daily iptacopan in adult PNH patients who have Hb≥10 g/dL in response to anti-C5 antibody and switch to iptacopan (Novartis)Pending enrollment
(pdf – password protected)
Polycythemia Vera
PI / ContactProtocol (Sponsor)Status
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
A Phase 2a Study of ISIS 702843 in Phlebotomy Dependent Polycythemia Vera Patients (ISIS 702843-CS4) (Ionis Pharmaceuticals)Open to enrollment
(pdf – password protected)
PI: Stephen Oh
Contact: Karyn Gordon
kdgordon@wustl.edu
314-362-0156
A Phase 3b Study of Ropeginterferon (P1101) in Polycythemia Vera Patients (PharmaEssentia)Pending Open
(pdf – password protected)
Sickle Cell Disease
PI / ContactProtocol (Sponsor)Status
PI: Allison King
Contact: Lisa Garrett
garrett_l@wustl.edu
314-362-0051
Sickle Cell Disease Patient Registry (SCDIC-II) (NHLBI)Enrolling
(pdf – password protected)
PI: Allison King
Contact: Lisa Garrett
garrett_l@wustl.edu
314-362-0051
The Epidemiology of Silent and Overt Strokes in Adults with Sickle Cell Disease (Global Blood Therapeutics)Enrolling
(pdf – password protected)
PI: Allison King
Contact: Lisa Garrett
garrett_l@wustl.edu
314-362-0051
Sickle Cell Disease and CardiovAscular Risk-Red cell Exchange Trial (SCD-CARRE) (NHLBI)Enrolling
(pdf – password protected)
PI: Sana Saif Ur Rehman
Contact: Isuru Gamlath
isuru.gamlath@wustl.edu
314-362-9998
Patient Characteristics and Treatment Patterns from Early Crizanlizumab Use in Real-world Setting (National Alliance of Sickle Cell Centers)(pdf – password protected)
PI: Sana Saif Ur Rehman
Contact: Isuru Gamlath
isuru.gamlath@wustl.edu
314-362-9998
Globin research Network for DATA and Discovery (GRNDaD) (Global Blood Therapeutics)(pdf – password protected)
PI: Sana Saif Ur Rehman
Contact: Isuru Gamlath
isuru.gamlath@wustl.edu
314-362-9998
Globin research Network for DATA and Discovery (GRNDaD) substudy – HUGS (Global Blood Therapeutics)(pdf – password protected)
Systemic Mastocytosis
PI / ContactProtocol (Sponsor)Status
PI: Stephen Oh
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 2 Study of CGT9486 in Patients with Nonadvanced Systemic Mastocytosis (Summit) (Cogent Biosciences)Open to enrollment
(pdf – password protected)
PI: Stephen Oh
Contact: Nicole Gaudin
nrgaudin@wustl.edu
314-747-7960
A Phase 2 Study of Avapritinib (BLU-285) in Nonadvanced Systemic Mastocytosis Patients with Inadequately Controlled Symptoms (BLU-285-2203) (Blueprint Medicines)Ongoing; closed to enrollment
(pdf – password protected)
Von Willebrand Disease
PI / ContactProtocol (Sponsor)Status
PI: Elaine Majerus
Contact: Sabrina Barber
s.barber@wustl.edu
314-273-1440
A Natural History Cohort Study of the Safety, Effectiveness, and Practice of Treatment for People with Severe Von Willebrand Disease (VWD) (American Thrombosis and Hemostasis Network (ATHN))Open to enrollment
(pdf – password protected)